Preprint / Version 1

Overcoming Barriers to Immunotherapy Treatment in AML

##article.authors##

  • Medha Nemani Polygence Student
  • Zachary Reinstein

DOI:

https://doi.org/10.58445/rars.984

Keywords:

AML, Immunotherapy, CAR T cells

Abstract

Acute Myeloid Leukemia (AML) is an aggressive cancer with poor prognosis and limited therapies. In particular, it has met with numerous challenges in the development of promising chimeric antigen receptor (CAR) T cell therapy and other emerging immunotherapies. Current standard of care has a high rate of resistance and relapse. The most significant challenge with CAR T cells is finding a suitable antigen target for AML. Several antigen targets including CD33, CD123, CD7, CLL1, FLT3 have been considered and tested in clinical trials but also have potential problems such as on-target off-tumor toxicity. Additionally, new technologies such as SynNotch CARs, the inducible caspase 9 suicide gene, and bi-specific T cell/NK cell engagers are being introduced to ensure more specific and/or complete eradication of AML.

 

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2024-02-24